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NEW BOOK
LATEST NEWS
Capricor's Shares Drop After FDA Rejects Deramiocel Cell Therapy for Heart Disease in DMD
Capricor Therapeutics faced a significant setback on July 11, 2025, when the FDA rejected its cell therapy, Deramiocel , for treating...
2 days ago
FDA Rejects Ultragenyx's Gene Therapy for Rare Disease - Sanfilippo Syndrome
The FDA has declined to approve Ultragenyx Pharmaceutical's gene therapy, UX111, for treating Sanfilippo syndrome type A, a rare genetic...
2 days ago
Biogen's Salanersen Shows Promise for SMA Patients Post-Gene Therapy
Biogen’s experimental drug, Salanersen, is showing promising potential for treating children with spinal muscular atrophy (SMA), even...
Jul 1
GENE TECH TIMES
The Future Has Arrived
New Gene-Editing Technique: A Better Alternative to CRISPR for Fixing Cystic Fibrosis Mutation
A team from the Broad Institute of MIT and Harvard, along with Harvard University and the Howard Hughes Medical Institute, has made...
Sep 11, 2024
New Gene Therapy Breakthrough Paves Way for Better Treatment of Brain Disorders
In a project funded by the National Institute of Mental Health (NIMH) and the National Institute of Neurological Disorders and Stroke...
Aug 20, 2024
FDA Approves BEQVEZ: A Breakthrough One-Time Gene Therapy for Adults with Hemophilia B
Gene therapy is transforming the landscape of treatment options, and the recent FDA approval of BEQVEZ marks a significant milestone for...
May 1, 2024
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