Past research has long suggested the significant impact of the microbiome on the efficacy of various anticancer treatments, including...

In an inspiring breakthrough for cancer treatment, a woman who underwent an experimental immunotherapy trial as a child has now been in...

A groundbreaking new approach in cancer treatment has emerged, utilizing light to disable the mitochondria, the energy-producing...

Hypophosphatasia (HPP), or "soft bone disease" is a rare genetic disorder that impacts bone and tooth development, leading to weak bones...

Several clinical trials in 2025 are pushing the boundaries of gene and cell therapy, aiming to address a range of complex diseases. Below...

Vertex Pharmaceuticals has announced a pivotal milestone for its VX-880 therapy, a stem-cell-derived islet cell treatment to restore...

Novartis's gene therapy, Zolgensma, is already approved in the U.S. for children under the age of two with spinal muscular atrophy (SMA),...

A recent international study has shown that lenadogene nolparvovec, a gene therapy based on adeno-associated virus (AAV), can provide...

As CRISPR-based therapies edge closer to becoming mainstream, groundbreaking treatments for blood disorders and cancer are making their...

Oxygen levels are a critical but often overlooked factor in scientific research. Conventionally, researchers grow cells at atmospheric...

Heart failure, which affects over 64 million people worldwide, is currently considered irreversible without a heart transplant....

Sickle cell disease (SCD), which affects over 100,000 people in the U.S., is about to see a major shift in treatment accessibility. With...

Governor Kathy Hochul has announced New York Biogenesis Park, a $430 million cell and gene therapy hub set to transform the field on Long...

Heart disease is a leading cause of death worldwide, affecting millions at every stage of life, including infants born with congenital...

The FDA has approved Regenecyte, an innovative therapy made from umbilical cord blood stem cells, to help rebuild blood and immune...

A clinical trial for NGN-401, a gene therapy designed to treat Rett syndrome, recently faced a setback when a young participant...

Gene therapy has shown promise in treating many genetic diseases, but some conditions, like muscular dystrophy, involve very large genes...

Imagine controlling genes with the precision of a light switch— controlling specific parts of the body as you will. That’s what the...

A recent 6-year checkup on boys treated with gene therapy for cerebral adrenoleukodystrophy (CALD) reveals lasting benefits for most...

In exciting news for Parkinson’s disease research, MeiraGTx has announced positive results from a Phase 2 clinical bridging study of...