Gene therapy treats respiratory diseases by targeting their genetic causes. This approach typically involves delivering therapeutic genes to the airway epithelium, which is crucial for lung function.
Key Mechanisms:
Gene Delivery: Gene therapy uses viral vectors like adeno-associated viruses (AAV) to introduce functional genes into affected lung cells.
Restoring Function: The introduced genes produce essential proteins, such as the CFTR protein in cystic fibrosis, which helps regulate ion transport and mucus clearance.
Research and Development: Ongoing studies aim to improve delivery methods and ensure the safety and effectiveness of gene therapies for respiratory conditions.
Got more to add on this topic? Share your thoughts in the comments below!
Comentários